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Utilizing CRISPR-Cas13d-knockdown in zebrafish to study a rare monogenic bone fragility syndrome

Year of publication

2025

Authors

Määttä, Kirsi; Chen, Yu-Chia; Pihlström, Sandra; Mäkitie, Riikka E.; Dambroise, Emilie; Legeai-Mallet, Laurence; Panula, Pertti; Mäkitie, Outi; Pekkinen, Minna

Organizations and authors

University of Helsinki

Määttä Kirsi

Pekkinen Minna

Mäkitie Outi

Panula Pertti

Mäkitie Riikka E.

Pihlström Sandra

Chen Yu-Chia

Helsinki University Hospital

Määttä Kirsi

Pekkinen Minna

Mäkitie Outi

Panula Pertti

Mäkitie Riikka E.

Pihlström Sandra

Chen Yu-Chia

Publication type

Publication format

Article

Report

No

Parent publication type

Journal

Article type

Original article

Audience

Scientific

Peer-reviewed

Peer-Reviewed

MINEDU's publication type classification code

A1 Journal article (refereed), original research

Publication channel information

Journal/Series

JBMR plus

Parent publication name

JBMR plus

Volume

9

Issue

11

Article number

ziaf153

​Publication forum

86825

​Publication forum level

1

Open access

Open access in the publisher’s service

Yes

Open access of publication channel

Fully open publication channel

Self-archived

Yes

License of the self-archived publication

CC BY

Other information

Fields of science

Biomedicine

Identified topic

[object Object]

Publication country

United Kingdom

Internationality of the publisher

International

Language

English

International co-publication

Yes

Co-publication with a company

No

DOI

10.1093/jbmrpl/ziaf153

The publication is included in the Ministry of Education and Culture’s Publication data collection

Yes